Vismodegib
/api/v1/drug/vismodegibBoxed warning
EMBRYO-FETAL TOXICITY ERIVEDGE can cause embryo-fetal death or severe birth defects when administered to a pregnant woman. ERIVEDGE is embryotoxic, fetotoxic, and teratogenic in animals. Teratogenic effects included severe midline defects, missing digits, and other irreversible malformations [see Warnings and Precautions (5.1) , Use in Specific Populations (8.1) ] . Verify the pregnancy status of females of reproductive potential within 7 days prior to initiating ERIVEDGE. Advise pregnant women of the potential risks to a fetus. Advise females of reproductive potential to use effective contraception during and after ERIVEDGE [ see Dosage and Administration (2.1) , Warnings and Precautions (5.1) , Use in Specific Populations (8.1 , 8.3) ] . Advise males of the potential risk of ERIVEDGE exposure through semen and to use condoms with a pregnant partner or a female partner of reproductive potential [see Warnings and Precautions (5.1) , Use in Specific Populations (8.3) ] . WARNING: EMBRYO-FETAL TOXICITY See full prescribing information for complete boxed warning. ERIVEDGE can cause embryo-fetal death or severe birth defects when administered to a pregnant woman. ERIVEDGE is embryotoxic, fetotoxic, and teratogenic in animals. Teratogenic effects included severe midline defects, missing digits, and other irreversible malformations.
Mechanism of action
Sourced from openFDAVismodegib is an inhibitor of the Hedgehog pathway. Vismodegib binds to and inhibits Smoothened, a transmembrane protein involved in Hedgehog signal transduction.
Indications
Sourced from openFDA- ERIVEDGE is indicated for the treatment of adults with metastatic basal cell carcinoma, or with locally advanced basal cell carcinoma that has recurred following surgery or who are not candidates for surgery and who are not candidates for radiation. ERIVEDGE ® (vismodegib) is a hedgehog pathway inhibitor indicated for the treatment of adults with metastatic basal cell carcinoma, or with locally advanced basal cell carcinoma that has recurred following surgery or who are not candidates for surgery and who are not candidates for radiation.
Contraindications
Sourced from openFDA- None. None.contraindicated
Dosage & administration
Sourced from openFDAThe recommended dosage is 150 mg orally once daily. ( 2 ) 2.1 Important Safety Information Verify pregnancy status of females of reproductive potential within 7 days prior to initiating ERIVEDGE [see Use in Specific Populations (8.1 , 8.3) ] . 2.2 Recommended Dosage The recommended dosage of ERIVEDGE is 150 mg taken orally once daily, with or without food, until disease progression or until unacceptable toxicity . Swallow capsules whole. Do not open or crush capsules . If a dose of ERIVEDGE is missed, resume dosing with the next scheduled dose. 2.3 Dosage Modifications for Adverse Reactions Withhold ERIVEDGE for up to 8 weeks for intolerable adverse reactions until improvement or resolution. Treatment durations shorter than 8 weeks prior to interruptions have not been studied. Permanently discontinue ERIVEDGE if patients experience severe cutaneous adverse reactions (SCARs) including Stevens-Johnson syndrome (SJS), toxic epidermal necrolysis (TEN), or drug reaction with eosinophilia and systemic symptoms (DRESS) [see Warnings and Precautions (5.2) ] . Interrupt ERIVEDGE for severe or intolerable musculoskeletal adverse reactions. Permanently discontinue ERIVEDGE for recurrent, severe or intolerable musculoskeletal adverse reactions [see Warnings and Precautions (5.3) ] .
Warnings & precautions
Sourced from openFDAEmbryo-Fetal Toxicity: Advise patients not to donate blood or blood products while receiving ERIVEDGE and for 24 months after the final dose of ERIVEDGE ( 5.1 ) Advise males not to donate semen during and for 3 months after therapy ( 5.1 , 8.3 ) Severe Cutaneous Adverse Reactions: Permanently discontinue ERIVEDGE in patients with these reactions ( 5.2 ) Musculoskeletal Adverse Reactions: Temporary dose interruption or discontinuation may be required for these reactions ( 5.3 ) Premature fusion of the epiphyses ( 5.4 , 8.4 ) 5.1 Embryo-Fetal Toxicity Based on its mechanism of action, ERIVEDGE can cause embryo-fetal death or severe birth defects when administered to a pregnant woman. In animal reproduction studies, vismodegib was embryotoxic, fetotoxic, and teratogenic at maternal exposures lower than the human exposures at the recommended dose of 150 mg once daily [see Use in Specific Populations (8.1) ] . Females of Reproductive Potential Verify the pregnancy status of females of reproductive potential within 7 days prior to initiating ERIVEDGE. Advise pregnant women of the potential risk to a fetus. Advise females of reproductive potential to use effective contraception during therapy with ERIVEDGE and for 24 months after the final dose [see Use in Specific Populations (8.1 , 8.3) ]. Males Vismodegib is present in semen. It is not known if the amount of vismodegib in semen can cause embryo-fetal harm.
Adverse reactions
Sourced from openFDAThe following clinically significant adverse reactions are described elsewhere in the labeling: Embryo-Fetal Toxicity [see Warnings and Precautions (5.1) ] Severe Cutaneous Adverse Reactions [see Warnings and Precautions (5.2) ] Musculoskeletal Adverse Reactions [see Warnings and Precautions (5.3) ] Premature Fusion of the Epiphyses [see Warnings and Precautions (5.4) ] The most common adverse reactions (incidence of ≥ 10%) are muscle spasms, alopecia, dysgeusia, weight loss, fatigue, nausea, diarrhea, decreased appetite, constipation, arthralgias, vomiting, and ageusia. To report SUSPECTED ADVERSE REACTIONS, contact Genentech, Inc. at 1-888-835-2555 or FDA at 1-800-FDA-1088 or www.fda.gov/medwatch . 6.1 Clinical Trials Experience Because clinical trials are conducted under widely varying conditions, adverse reaction rates observed in the clinical trials of a drug cannot be directly compared to rates in the clinical trials of another drug and may not reflect the rates observed in clinical practice. The safety data described below reflect exposure to ERIVEDGE in 138 patients with advanced basal cell carcinoma (BCC) who received ERIVEDGE at doses ≥ 150 mg orally daily in four open-label, uncontrolled, dose-ranging or fixed single dose clinical trials [Study SHH3925g, SHH4437g, SHH4476g and SHH4610g]. The median age of these patients was 61 years (range 21 to 101 years), 100% were White (including Hispanics), and 64% were male. The median duration of treatment was approximately 10 months (range 21 days to 36 months); 111 patients received ERIVEDGE for 6 months or longer.
Use in specific populations
Sourced from openFDALactation: Breastfeeding not recommended. ( 8.2 ) Females and Males of Reproductive Potential: May cause amenorrhea in females. ( 8.3 ) 8.1 Pregnancy Pregnancy Exposure Registry There is a pregnancy exposure registry that monitors pregnancy outcomes in women exposed to ERIVEDGE during pregnancy. Report pregnancies to Genentech at 1-888-835-2555. Risk Summary Based on its mechanism of action and findings from animal reproduction studies, ERIVEDGE can cause fetal harm when administered to a pregnant woman [see Clinical Pharmacology (12.1) ] . In animal reproduction studies, oral administration of vismodegib during organogenesis at doses below the 150 mg clinical dose resulted in embryotoxicity, fetotoxicity, and teratogenicity in rats (see Data ) . There are no human data on the use of ERIVEDGE in pregnant women. Advise pregnant women of the potential risk to a fetus. In the U.S. general population, the estimated background risk of major birth defects and miscarriage in clinically recognized pregnancies is 2-4% and 15-20%, respectively. Data Animal Data In an embryo-fetal toxicity study, pregnant rats were administered vismodegib orally at doses of 10, 60, or 300 mg/kg/day during the period of organogenesis.
Pharmacokinetics
Sourced from openFDA- Metabolism
- The pharmacokinetics of vismodegib were studied in healthy subjects and patients. Following daily oral dosing, the pharmacokinetics of vismodegib appear to be nonlinear with steady state achieved within 7 days.
Approval history
Sourced from openFDA- Jan 30, 2012NDANDA203388Genentech
FAERS reports
- 1Muscle Spasms2,04223%
- 2Alopecia1,39216%
- 3Ageusia1,00211%
- 4Fatigue96111%
- 5Dysgeusia7458.5%
- 6Death7408.4%
- 7Weight Decreased7328.3%
- 8Nausea7068.1%
- 9Decreased Appetite7008.0%
- 10Diarrhoea4705.4%
- 11Constipation3784.3%
- 12Off Label Use3694.2%
- 13Asthenia2923.3%
- 14Arthralgia2793.2%
- 15No Adverse Event2572.9%
Clinical trials
The 10 most recently updated of 92 ClinicalTrials.gov registrations naming Vismodegib as an intervention. Registration is not evidence of efficacy or safety — reference crosswalk only.
- Targeted Therapy Directed by Genetic Testing in Treating Patients With Advanced Refractory Solid Tumors, Lymphomas, or Multiple Myeloma (The MATCH Screening Trial)Active not recruiting · Phase 2 · Interventional · 6,452 enrolled · National Cancer Institute (NCI)NCT02465060updated 2026-06-03
- Vismodegib, FAK Inhibitor GSK2256098, Capivasertib, and Abemaciclib in Treating Patients With Progressive MeningiomasRecruiting · Phase 2 · Interventional · 124 enrolled · Alliance for Clinical Trials in OncologyNCT02523014updated 2026-06-02
- Testing GDC-0449 (Vismodegib) as Potentially Targeted Treatment in Cancers With Smoothened or Patched 1 Mutant Tumors (MATCH - Subprotocol T)Active not recruiting · Phase 2 · Interventional · 34 enrolled · National Cancer Institute (NCI)NCT06357988updated 2026-05-28
- Relationship Between Pharmacokinetics and Safety of Vismodegib - OPTIVISMO-1Completed · Phase 4 · Interventional · 27 enrolled · University Hospital, BordeauxNCT03610022updated 2026-05-19
- A Study Evaluating the Efficacy and Safety of Vismodegib (GDC-0449, Hedgehog Pathway Inhibitor) in Patients With Advanced Basal Cell CarcinomaCompleted · Phase 2 · Interventional · 104 enrolled · Genentech, Inc.NCT00833417updated 2026-05-11
- A Study of Vismodegib (GDC-0449) in Patients Treated With Vismodegib in a Previous Genentech-sponsored Phase I or II Cancer StudyCompleted · Phase 2 · Interventional · 19 enrolled · Genentech, Inc.NCT00959647updated 2026-05-08
- Study Evaluating the Interest of Vismodegib as Neo-adjuvant Treatment of Basal Cell Carcinoma (BCC)Completed · Phase 2 · Interventional · 55 enrolled · University Hospital, LilleNCT02667574updated 2026-04-22
- GDC-0449 and Erlotinib Hydrochloride With or Without Gemcitabine Hydrochloride in Treating Patients With Metastatic Pancreatic Cancer or Solid Tumors That Cannot Be Removed by SurgeryActive not recruiting · Phase 1 · Interventional · 55 enrolled · National Cancer Institute (NCI)NCT00878163updated 2026-04-13
- Vismodegib in Treating Patients With Advanced ChondrosarcomasActive not recruiting · Phase 2 · Interventional · 45 enrolled · National Cancer Institute (NCI)NCT01267955updated 2026-04-13
- Adaptive Therapy of Vismodegib in Advanced Basal Cell CarcinomaRecruiting · Early phase 1 · Interventional · 34 enrolled · H. Lee Moffitt Cancer Center and Research InstituteNCT05651828updated 2026-04-01
Frequently asked questions
- How does Vismodegib work?
- Vismodegib is an inhibitor of the Hedgehog pathway. Vismodegib binds to and inhibits Smoothened, a transmembrane protein involved in Hedgehog signal transduction.
- What is Vismodegib used for?
- According to FDA labeling, Vismodegib carries indications including: ERIVEDGE is indicated for the treatment of adults with metastatic basal cell carcinoma, or with locally advanced basal cell carcinoma that has recurred following surgery or who are not candidates for surgery and who are not candidates for radiation. ERIVEDGE ® (vismodegib) is a hedgehog pathway inhibitor indicated for the treatment of adults with metastatic basal cell carcinoma, or with locally advanced basal cell carcinoma that has recurred following surgery or who are not candidates for surgery and who are not candidates for radiation.. This is a reference summary of labeled uses, not medical advice or a treatment recommendation.
- What class of drug is Vismodegib?
- Vismodegib is classified as Hedgehog pathway inhibitors, Hedgehog Pathway Inhibitor, Smoothened Receptor Antagonists.
- What are the brand names for Vismodegib?
- Vismodegib is marketed under brand names including Erivedge.
- What are the contraindications for Vismodegib?
- Vismodegib labeling lists contraindications including: None. None.. Always consult the full prescribing information and a clinician.
vismodegib is illustrative MVP content compiled from public sources. pharmacopeia is for educational and informational use only and is not a substitute for professional medical advice.